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CAMP4 Therapeutics

CAMP4 Therapeutics

Biotechnology company

Appears in 1 story

Stories

First treatment for SYNGAP1 genetic disorder enters human testing

New Capabilities

Sponsor of the CMP-002 trial

About 700 people worldwide have a confirmed diagnosis of SYNGAP1-related disorder. It causes intellectual disability and seizures, and no drug has ever been approved to treat it. On July 27, 2026, that changed at the edges: Australia's drug regulator cleared the first medicine designed to fix the disorder's root cause to be tested in people.

Updated Yesterday