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Sarepta Therapeutics

Sarepta Therapeutics

Biotechnology Company

Appears in 1 story

Stories

The race to build a better Duchenne therapy

New Capabilities

Incumbent leader facing safety setbacks

Boys born with Duchenne muscular dystrophy typically lose the ability to walk before their teens and rarely live past 30. The first drugs designed to slow that decline reached the market in 2016, but they restore less than 1% of normal dystrophin, the muscle protein patients are missing. A decade later, a new wave of biotech companies is trying to deliver far more of that protein into muscle cells using engineered molecular shuttles.

Updated 2 hours ago