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BioMarin Pharmaceutical

BioMarin Pharmaceutical

Biopharmaceutical Company

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Race to replace injections for childhood dwarfism

New Capabilities

Market leader with only approved achondroplasia treatment

About 250,000 people worldwide have achondroplasia, the most common genetic cause of dwarfism. Until BioMarin's Voxzogo, the only approved treatment required daily injections.

Updated May 29