Gene therapy company
Appears in 1 story
Sponsor of AMT-130; BLA and MAA under review, four-year data reported September 29, 2026
uniQure reported four-year data from its Huntington's gene therapy trial on September 29. The results were mixed: the main composite measure showed 44% slower decline, short of statistical significance, while a functional-capacity measure showed 61% slower decline.
Updated Oct 1
No stories match your search
Try a different keyword
How would you like to describe your experience with the app today?
